Browsing by Author Rafferty, G
Showing results 1 to 2 of 2
Issue Date | Title | Author(s) |
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7-Jun-2022 | INCEPTUS Natural History, Run-in Study for Gene Replacement Clinical Trial in X-Linked Myotubular Myopathy | Dowling, JJ; Müller-Felber, W; Smith, BK; Bönnemann, CG; Kuntz, NL; Muntoni, F; Servais, L; Alfano, LN; Beggs, AH; Bilder, DA; Blaschek, A; Duong, T; Graham, RJ; Jain, M; Lawlor, MW; Lee, J; Coats, J; Lilien, C; Lowes, LP; MacBean, V; Neuhaus, S; Noursalehi, M; Pitts, T; Finlay, C; Christensen, S; Rafferty, G; Seferian, AM; Tsuchiya, E; James, ES; Miller, W; Sepulveda, B; Vila, MC; Prasad, S; Rico, S; Shieh, PB |
5-Sep-2018 | INCEPTUS pre-phase 1, prospective, non-interventional, natural history run-in study to evaluate subjects aged 3-years and younger with X-linked myotubular myopathy: preliminary findings | Shieh, P; Mueller-Felber, W; Smith, B; Bonnemann, C; Dowling, J; Kuntz, N; Muntoni, F; Servais, L; Bilder, D; Duong, T; Graham, R; Jain, M; Lawlor, M; MacBean, V; Noursalehi, M; Pitts, T; Rafferty, G; Rico, S; Prasad, S |