Browsing by Author Bonnemann, C
Showing results 1 to 2 of 2
Issue Date | Title | Author(s) |
---|---|---|
1-May-2022 | Improved Respiratory Outcomes for X-Linked Myotubular Myopathy (XLMTM) with Gene Replacement Therapy, Resamirigene Bilparvovec (ASPIRO): Preliminary Results from ASPIRO, a Phase 1/2/3 Study | Perez, GF; Shieh, P; Kuntz, N; Dowling, J; Mueller-Felber, W; Blaschek, A; Bonnemann, C; Foley, A; Saade, D; Seferian, A; Servais, L; Lawlor, M; MacBean, V; Coats, J; Han, C; Lee, J; Noursalehi, M; Prasad, S; Rico, S; Miller, W; Graham, R |
5-Sep-2018 | INCEPTUS pre-phase 1, prospective, non-interventional, natural history run-in study to evaluate subjects aged 3-years and younger with X-linked myotubular myopathy: preliminary findings | Shieh, P; Mueller-Felber, W; Smith, B; Bonnemann, C; Dowling, J; Kuntz, N; Muntoni, F; Servais, L; Bilder, D; Duong, T; Graham, R; Jain, M; Lawlor, M; MacBean, V; Noursalehi, M; Pitts, T; Rafferty, G; Rico, S; Prasad, S |