Browsing by Author Perez, GF
Showing results 1 to 2 of 2
Issue Date | Title | Author(s) |
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16-Sep-2024 | An algorithm for discontinuing mechanical ventilation in boys with x-linked myotubular myopathy after positive response to gene therapy: the ASPIRO experience | Graham, RJ; Amin, R; Demirel, N; Edel, L; Lilien, C; MacBean, V; Rafferty, GF; Sawnani, H; Schon, C; Smith, BK; Syed, F; Sarazen, M; Prasad, S; Rico, S; Perez, GF |
1-May-2022 | Improved Respiratory Outcomes for X-Linked Myotubular Myopathy (XLMTM) with Gene Replacement Therapy, Resamirigene Bilparvovec (ASPIRO): Preliminary Results from ASPIRO, a Phase 1/2/3 Study | Perez, GF; Shieh, P; Kuntz, N; Dowling, J; Mueller-Felber, W; Blaschek, A; Bonnemann, C; Foley, A; Saade, D; Seferian, A; Servais, L; Lawlor, M; MacBean, V; Coats, J; Han, C; Lee, J; Noursalehi, M; Prasad, S; Rico, S; Miller, W; Graham, R |