Brunel University Research Archive(BURA) preserves and enables easy and open access to all
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Browsing by Author Seferian, A
Showing results 1 to 2 of 2
| Issue Date | Title | Author(s) |
|---|---|---|
| 18-Sep-2025 | Gene therapy for children with X-linked myotubular myopathy: a plain language summary of publication for the ASPIRO study | Shieh, P; Hughes, W; Wood, M; Beggs, A; Lawlor, M; Coats, J; Varfaj, F; Graham, R; Kuntz, N; Dowling, J; Muller-Felber, W; Bonnemann, C; Buj Bello, A; Servais, L; MacBean, V; Muntoni, F; Foley, AR; Blaschek, A; James, E; Seferian, A; Alfano, L; Duong, T; Noursalehi, M; Miller, W; Lee, J; Prasad, S; Rico, S |
| 1-May-2022 | Improved Respiratory Outcomes for X-Linked Myotubular Myopathy (XLMTM) with Gene Replacement Therapy, Resamirigene Bilparvovec (ASPIRO): Preliminary Results from ASPIRO, a Phase 1/2/3 Study | Perez, GF; Shieh, P; Kuntz, N; Dowling, J; Mueller-Felber, W; Blaschek, A; Bonnemann, C; Foley, A; Saade, D; Seferian, A; Servais, L; Lawlor, M; MacBean, V; Coats, J; Han, C; Lee, J; Noursalehi, M; Prasad, S; Rico, S; Miller, W; Graham, R |