1. Brunel University Research Archive
  2. College of Health, Medicine and Life Sciences
  3. Dept of Health Sciences
  4. Dept of Health Sciences Embargoed Research Papers
Please use this identifier to cite or link to this item: http://bura.brunel.ac.uk/handle/2438/31987
Full metadata record
DC FieldValueLanguage
dc.contributor.authorShieh, P-
dc.contributor.authorHughes, W-
dc.contributor.authorWood, M-
dc.contributor.authorBeggs, A-
dc.contributor.authorLawlor, M-
dc.contributor.authorCoats, J-
dc.contributor.authorVarfaj, F-
dc.contributor.authorGraham, R-
dc.contributor.authorKuntz, N-
dc.contributor.authorDowling, J-
dc.contributor.authorMuller-Felber, W-
dc.contributor.authorBonnemann, C-
dc.contributor.authorBuj Bello, A-
dc.contributor.authorServais, L-
dc.contributor.authorMacBean, V-
dc.contributor.authorMuntoni, F-
dc.contributor.authorFoley, AR-
dc.contributor.authorBlaschek, A-
dc.contributor.authorJames, E-
dc.contributor.authorSeferian, A-
dc.contributor.authorAlfano, L-
dc.contributor.authorDuong, T-
dc.contributor.authorNoursalehi, M-
dc.contributor.authorMiller, W-
dc.contributor.authorLee, J-
dc.contributor.authorPrasad, S-
dc.contributor.authorRico, S-
dc.date.accessioned2025-09-13T14:47:59Z-
dc.date.available2025-09-13T14:47:59Z-
dc.date.issued2025-
dc.identifierORCiD: Victoria MacBean https://orcid.org/0000-0003-0268-2693-
dc.identifier.citationShieh, P. et al. (2025) 'Gene therapy for children with X-linked myotubular myopathy: a plain language summary of publication for the ASPIRO study', Therapeutic Advances in Rare Disease, 0 (accepted, in press)en_US
dc.identifier.issn2633-0040-
dc.identifier.urihttps://bura.brunel.ac.uk/handle/2438/31987-
dc.description...en_US
dc.description.abstract...en_US
dc.description.sponsorship...en_US
dc.format.extent1 - 9-
dc.format.mediumElectronic-
dc.language.isoen_USen_US
dc.publisherSAGE Publicationsen_US
dc.subjectgene therapyen_US
dc.subjectX-linked myotubular myopathyen_US
dc.subjectresamirigene bilparvovecen_US
dc.titleGene therapy for children with X-linked myotubular myopathy: a plain language summary of publication for the ASPIRO studyen_US
dc.typeArticleen_US
dc.relation.isPartOfTherapeutic Advances in Rare Disease-
pubs.issue0-
pubs.publication-statusAccepted-
pubs.volume00-
dc.identifier.eissn2633-0040-
Appears in Collections:Dept of Health Sciences Embargoed Research Papers

Files in This Item:
File Description SizeFormat 
ASPIRO PLSP Draft 5_04Apr2025 (1).pdfEmbargoed until publication617.25 kBAdobe PDFView/Open
Show simple item record


Items in BURA are protected by copyright, with all rights reserved, unless otherwise indicated.